TerminatedPHASE1, PHASE2NCT03952156
Gene Therapy Clinical Study in Adult PKU
Studying Disorder of phenylalanin or tyrosine metabolism
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Homology Medicines, Inc
- Principal Investigator
- Olaf A Bodamer, M.D.Boston Children's Hospital
- Intervention
- HMI-102(genetic)
- Enrollment
- 10 enrolled
- Eligibility
- 18-55 years · All sexes
- Timeline
- 2019 – 2023
Study locations (13)
- Kaiser Permanente Los Angeles Medical Center, Los Angeles, California, United States
- Children's Hospital of Orange County, Orange, California, United States
- University of South Florida, Tampa, Florida, United States
- Emory University Hospital, Atlanta, Georgia, United States
- Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Icahn School of Medicine at Mount Sinai, New York, New York, United States
- The University of North Carolina At Chapel Hill, Chapel Hill, North Carolina, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- University of Texas Southwestern Medical Center, Dallas, Texas, United States
- University of Utah, Salt Lake City, Utah, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT03952156 on ClinicalTrials.gov