CompletedPHASE1, PHASE2NCT03811028
A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients
Studying Sanfilippo syndrome type A
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Swedish Orphan Biovitrum
- Principal Investigator
- Paul Harmatz, MD, M.D., Ph.DChildren´s Hospital and Research Center, Oakland
- Intervention
- SOBI003(drug)
- Enrollment
- 6 enrolled
- Eligibility
- All sexes
- Timeline
- 2019 – 2021
Study locations (3)
- Children´s Hospital and research center, Oakland, California, United States
- University of North Carolina hospitals, Chapel Hill, North Carolina, United States
- Gazi University Hospital, Ankara, Turkey (Türkiye)
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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