CompletedPHASE1, PHASE2NCT03720990
Smith-Lemli-Opitz Syndrome and Cholic Acid
Studying 46,XY difference of sex development due to a cholesterol synthesis defect
Last synced from ClinicalTrials.gov
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- Sponsor
- University of Nebraska
- Principal Investigator
- Ellen R Elias, MDUniversity of Colorado - Colorado Children's Hospital
- Intervention
- Cholic Acid(drug)
- Enrollment
- 12 enrolled
- Eligibility
- 2-25 years · All sexes
- Timeline
- 2021 – 2023
Study locations (2)
- Colorado Children's Hospital, Aurora, Colorado, United States
- University of Nebraska Medical Center, Omaha, Nebraska, United States
Collaborators
University of Colorado, Denver · Children's Hospital Medical Center, Cincinnati · University of Pittsburgh
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT03720990 on ClinicalTrials.gov