Active, not recruitingPHASE1, PHASE2NCT03639701
Treatment of TK2 Deficiency With Thymidine and Deoxycytidine
Studying Mitochondrial DNA depletion syndrome
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Columbia University
- Principal Investigator
- Michio Hirano, MD, M.DColumbia University
- Intervention
- Thymidine(drug)
- Enrollment
- 23 enrolled
- Eligibility
- All sexes
- Timeline
- 2017 – 2026
Study locations (1)
- Columbia University Irving Medical Center, New York, New York, United States
Collaborators
Muscular Dystrophy Association · Hospital Universitario 12 de Octubre · Instituto de Salud Carlos III · University of Seville · Medical Research Council Mitochondrial Biology Unit · Centro de Investigación Biomédica en Red Enfermedades Raras (CIBERER), Spain · Hospitales Universitarios Virgen del Rocío · Universitat Autonoma de Barcelona
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT03639701 on ClinicalTrials.gov