Active, not recruitingPHASE1, PHASE2NCT03588299
Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle"
Studying Hemophilia A
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Bayer
- Intervention
- BAY2599023 (DTX201)(drug)
- Enrollment
- 11 enrolled
- Eligibility
- 18 years · MALE
- Timeline
- 2018 – 2026
Study locations (13)
- Arkansas Children's Hospital - Hematology / Oncology, Little Rock, Arkansas, United States
- C.S. Mott Children's Hospital - Hematology / Oncology, Ann Arbor, Michigan, United States
- UW Health Carbone Cancer Center, Madison, Wisconsin, United States
- SHATHD Spec. Hospi. for Active Treatm. of Haematol. Dis. EAD, Sofia, Sofia City Province, Bulgaria
- CHU Rennes - Hopital Pontchaillou, Rennes, Brittany Region, France
- APHP-Hopital Necker Enfants malades, Paris, Île-de-France Region, France
- Universitätsklinikum des Saarlandes, Homburg, Saarland, Germany
- Vivantes Klinikum im Friedrichshain, Berlin, Germany
- Academisch Medisch Centrum (AMC), Amsterdam, North Holland, Netherlands
- Erasmus Medisch Centrum, Rotterdam, South Holland, Netherlands
- Universitair Medisch Centrum Groningen, Groningen, Netherlands
- University Medical Center Utrecht, Utrecht, Netherlands
- Manchester Royal Infirmary, Manchester, Greater Manchester, United Kingdom
Collaborators
Ultragenix pharmaceutical
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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