CompletedPHASE1, PHASE2NCT03300453
Intracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome
Studying Mucopolysaccharidosis type 3
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- UniQure Biopharma B.V.
- Principal Investigator
- Kumaran Deiva, MDHopitaux Universitaires Paris-Sud
- Intervention
- rAAV2/5-hNAGLU(drug)
- Enrollment
- 4 enrolled
- Eligibility
- All sexes
- Timeline
- 2013 – 2019
Study locations (1)
- Hopitaux Universitaires Paris-Sud, Paris, Le Kremlin-Bicetre Cedex, France
Collaborators
Venn Life Sciences · Institut Pasteur
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT03300453 on ClinicalTrials.gov