RecruitingPHASE2, PHASE3NCT02716246
Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH
Studying Sanfilippo Syndrome
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Ultragenyx Pharmaceutical Inc
- Principal Investigator
- Medical DirectorUltragenyx Pharmaceutical Inc
- Intervention
- UX111(biological)
- Enrollment
- 36 enrolled
- Eligibility
- All sexes
- Timeline
- 2016 – 2027
Study locations (5)
- Nationwide Children's Hospital, Columbus, Ohio, United States
- Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- Women's and Children's Hospital, North Adelaide, South Australia, Australia
- Vall d'Hebron Barcelona Hospital Campus, Barcelona, Barcelona, Spain
- Hospital Clínico Universitario de Santiago, Santiago de Compostela, Spain
Collaborators
Abeona Therapeutics, Inc
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT02716246 on ClinicalTrials.govOther trials for Sanfilippo Syndrome
Additional recruiting or active studies for the same condition.