RecruitingNCT02714764
Evaluation of Outcome Metrics in Alexander Disease
Studying Alexander disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Children's Hospital of Philadelphia
- Principal Investigator
- Amy Waldman, MDChildren's Hospital of Philadelphia
- Enrollment
- 200 enrolled
- Eligibility
- All sexes
- Timeline
- 2016 – 2030
Study locations (1)
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Collaborators
Ionis Pharmaceuticals, Inc. · University of Wisconsin, Madison · Pennsylvania Department of Health
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT02714764 on ClinicalTrials.govOther trials for Alexander disease
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