CompletedNCT01869270
Gene Therapy for Tay-Sachs Disease
Studying Gangliosidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- University of Minnesota
- Principal Investigator
- Chester B. Whitley, PhD, MDUniversity of Minnesota
- Enrollment
- 4 enrolled
- Eligibility
- All sexes
- Timeline
- 2010 – 2014
Study locations (2)
- Data Management and Coordinating Center (DMCC), Univ. of South Florida, Tampa, Florida, United States
- University of Minnesota, Minneapolis, Minnesota, United States
Collaborators
Rare Diseases Clinical Research Network · National Center for Advancing Translational Sciences (NCATS) · National Institute of Neurological Disorders and Stroke (NINDS) · National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT01869270 on ClinicalTrials.govOther trials for Gangliosidosis
Additional recruiting or active studies for the same condition.
- RECRUITINGPHASE3NCT07082543A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 GangliosidosisAzafaros A.G.
- RECRUITINGPHASE1, PHASE2NCT03952637A Phase 1/2 Study of Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 GangliosidosisNational Human Genome Research Institute (NHGRI)
- RECRUITINGNCT00668187A Natural History Study of the GangliosidosesUniversity of Minnesota