CompletedPhase 2NCT01212744
Safety, Tolerability, and Efficacy Study of rAvPAL-PEG Administered Daily in Subjects With Phenylketonuria (PKU)
Studying Classic phenylketonuria
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- BioMarin Pharmaceutical
- Principal Investigator
- Ari Gershman, MD, M.DBioMarin Pharmaceutical
- Intervention
- rAvPAL-PEG(drug)
- Enrollment
- 16 enrolled
- Eligibility
- 16-70 years · All sexes
- Timeline
- 2011 – 2015
Study locations (9)
- The Children's Hospital, Aurora, Colorado, United States
- University of Florida, Gainesville, Florida, United States
- Weisskopf Child Evaluation Center / University of Louisville, Louisville, Kentucky, United States
- University of Missouri, Columbia, Missouri, United States
- Washington University Center for Applied Research Sciences, St Louis, Missouri, United States
- Albany Medical Center, Albany, New York, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
- University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania, United States
- University of Wisconsin-Madison, Madison, Wisconsin, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT01212744 on ClinicalTrials.govOther trials for Classic phenylketonuria
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