CompletedPHASE2, PHASE3NCT00891306
Efficacy and Safety of Human Lipoprotein Lipase (LPL)[S447X] Expressed by an Adeno-Associated Viral Vector in LPL-deficient Subjects
Studying Familial lipoprotein lipase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Amsterdam Molecular Therapeutics
- Principal Investigator
- Daniel Gaudet, MD, Ph.D.ECOGENE-21 Clinical Trial Center / Centre de santé et de services sociaux de Chicoutimi, Chicoutimi Hospital, Quebec, Canada
- Intervention
- Alipogene Tiparvovec (AMT-011), Human LPL [S447X](genetic)
- Enrollment
- 5 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2009 – 2011
Study locations (2)
- ECOGENE-21 Clinical Trial Center / Centre de santé et de services sociaux de Chicoutimi, Chicoutimi, Quebec, Canada
- Centre des Maladies Lipidiques de Québec, Québec, Quebec, Canada
Collaborators
The Clinical Trial Company
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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