CompletedNCT00778206
PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry
Studying Classic phenylketonuria
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- BioMarin Pharmaceutical
- Principal Investigator
- Kristin Lindstrom, MD, M.DBioMarin Pharmaceutical
- Intervention
- Kuvan(drug)
- Enrollment
- 1887 enrolled
- Eligibility
- All sexes
- Timeline
- 2008 – 2021
Study locations (30)
- Childrens Hospital of Los Angeles, Los Angeles, California, United States
- LAC and USC Medical Center, Los Angeles, California, United States
- UCLA, Los Angeles, California, United States
- Children's Hospital of Orange County, Orange, California, United States
- University of California, San Diego, San Diego, California, United States
- Stanford University, Pediatrics, Stanford, California, United States
- Children's Hospital, University of Colorado School of Medicine, Aurora, Colorado, United States
- Children's National Medical Center, Washington D.C., District of Columbia, United States
- University of Florida, Gainesville, Florida, United States
- University of Miami, Miller School of Medicine, Department of Human Genetics, Miami, Florida, United States
- University of South Florida, Tampa, Florida, United States
- Tampa Children's Hospital, St. Joseph's Pediatric Endocrine Associates, Tampa, Florida, United States
- Emory University, Decatur, Georgia, United States
- Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Indiana University School of Medicine, Indianapolis, Indiana, United States
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT00778206 on ClinicalTrials.govOther trials for Classic phenylketonuria
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