Phase 1/2 Safety and Efficacy Study of AAV-RPE65 Vector to Treat Leber Congenital Amaurosis

Key facts

Sponsor

Beacon Therapeutics

Principal Investigator

J Timothy Stout, MD, PhD, MBA

Casey Eye Institute, Oregon Health & Science University

Intervention

rAAV2-CB-hRPE65(biological)

Enrollment

12 enrolled

Eligibility

6 years · All sexes

Timeline

2009 – 2017

Study locations (2)

• University of Massachusetts Medical School, Worcester, Massachusetts, United States
• Casey Eye Institue, Oregon Health & Science University, Portland, Oregon, United States

Collaborators

Oregon Health and Science University · University of Massachusetts, Worcester

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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