UnknownPhase 4NCT00487630

Evaluation of Efficacy and Safety of Agalsidase Beta in Heterozygous Females for Fabry Disease

Studying Fabry disease

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Key facts

Sponsor
Assistance Publique - Hôpitaux de Paris
Principal Investigator
Dominique P GERMAIN, MD, PhD
Centre de reference de la maladie de Fabry et des maladies hereditaires du tissu conjonctif. Assistance Publique Hopitaux de Paris
Intervention
recombinant alpha-galactosidase A(drug)
Enrollment
34 enrolled
Eligibility
15 years · FEMALE
Timeline
20052009

Study locations (1)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT00487630 on ClinicalTrials.gov

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