CompletedPhase 2NCT00483314
Homocystinuria: Treatment With N-Acetylcysteine
Studying Homocystinuria
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- McGill University Health Centre/Research Institute of the McGill University Health Centre
- Principal Investigator
- Brian M GILFIX, MD, PhDMcGill University Health Centre/Research Institute of the McGill University Health Centre
- Intervention
- N-acetylcysteine(drug)
- Enrollment
- 5 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2007 – 2009
Study locations (2)
- MUHC-Royal Victoria Hospital, Montreal, Quebec, Canada
- Royal Victoria Hospital, Montreal, Quebec, Canada
Collaborators
March of Dimes
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT00483314 on ClinicalTrials.govOther trials for Homocystinuria
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- ENROLLING BY INVITATIONPHASE3NCT06431893A Phase 3 Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE)Travere Therapeutics, Inc.
- ACTIVE NOT RECRUITINGPHASE3NCT06247085A Study to Investigate Efficacy and Safety of Pegtibatinase Compared With Placebo in Participants ≥12 to ≤65 Years of Age With Classical Homocystinuria (HCU) Due to Cystathionine Beta Synthase Deficiency Receiving Standard of Care TreatmentTravere Therapeutics, Inc.
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT03406611Pegtibatinase As an Enzyme Therapy for Patients with Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (COMPOSE)Travere Therapeutics, Inc.
- RECRUITINGNCT02998710Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)Travere Therapeutics, Inc.