CompletedPhase 2NCT00418847
Pharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis
Studying Gangliosidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- The Hospital for Sick Children
- Principal Investigator
- Joe TR Clarke, MDThe Hospital for Sick Children, Toronto Canada
- Intervention
- miglustat(drug)
- Enrollment
- 5 enrolled
- Eligibility
- 6-20 years · All sexes
- Timeline
- 2004 – 2009
Study locations (1)
- The Hospital for Sick Children, Toronto, Ontario, Canada
Collaborators
Actelion
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT00418847 on ClinicalTrials.govOther trials for Gangliosidosis
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- RECRUITINGPHASE1, PHASE2NCT03952637A Phase 1/2 Study of Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 GangliosidosisNational Human Genome Research Institute (NHGRI)
- RECRUITINGNCT00668187A Natural History Study of the GangliosidosesUniversity of Minnesota