Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

Key facts

Sponsor

Mirum Pharmaceuticals, Inc.

Principal Investigator

James Heubi, MD, MD

Children's Hospital Medical Center, Cincinnati

Intervention

Cholic Acids(drug)

Enrollment

85 enrolled

Eligibility

All sexes

Timeline

1992 – 2009

Study locations (1)

• Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

Collaborators

Children's Hospital Medical Center, Cincinnati

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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