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🏅 FDA Orphan Designation

LUXTURNA

voretigene neparvovec-rzyl

Manufacturer: Spark Therapeutics, Inc.

Indicated for:
OBSOLETE: Inherited retinal disorder

FDA-Approved Indications (1)

indicated for the treatment of patients with confirmed biallelic RPE65 mutation-associated retinal dystrophy

Population: all ages

Indications & Usage

1 INDICATIONS AND USAGE LUXTURNA (voretigene neparvovec-rzyl) is an adeno-associated virus vector-based gene therapy indicated for the treatment of patients with confirmed biallelic RPE65 mutation-associated retinal dystrophy. Patients must have viable retinal cells as determined by the treating physician(s). LUXTURNA is an adeno-associated virus vector-based gene therapy indicated for the treatment of patients with confirmed biallelic RPE65 mutation-associated retinal dystrophy. Patients must have viable retinal cells as determined by the treating physician(s). ( 1 )

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LUXTURNA
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Medical disclaimer: This information is for educational purposes only. Always consult a qualified healthcare provider before making treatment decisions. Data sourced from FDA and current as of our last update.