Pediatrics, Pediatric Hematology-Oncology

University of Minnesota Medical Center

Psychiatry & Neurology, Neurology

Massachusetts General Hospital

Rare Disease Specialist

UPMC Children's Hospital of Pittsburgh

Leipzig University Medical Center, Leukodystrophy Outpatient Clinic, Department of Neurology, Leipzig, Germany

Rare Disease Specialist

Children's Hospital of Philadelphia

Pediatrics, Pediatric Hematology-Oncology

New York Medical College

Bellvitge University Hospital

Children's Hospital Medical Center, Cincinnati

PTC Therapeutics

Children's Hospital Medical Center, Cincinnati

Rare Disease Specialist

Jagiellonian University Medical College, Department of Neurology

Boston Children's Hospital

Great Ormond Street Hospital for Chidren NHS Foundation Trust

Hôpital Bicêtre

Institut du Cerveau et de la Moëlle épinière

Pediatrics, Pediatric Hematology-Oncology

University of Florida

Kremlin Bicêtre Hôpital

Pediatrics, Pediatric Critical Care Medicine

bluebird bio, Inc.

Beijing Tiantan Hospital, Capital Medical University, Beijing, China

Hugo W. Moser Research Institute at Kennedy Krieger, Inc.

University of Leipzig

Pathology, Anatomic Pathology & Clinical Pathology

bluebird bio, Inc.

University of California, Los Angeles

Boston Children's Hospital