Pediatrics, Pediatric Hematology-Oncology

University of Minnesota Medical Center

Psychiatry & Neurology, Neurology

Massachusetts General Hospital

Leipzig University Medical Center, Leukodystrophy Outpatient Clinic, Department of Neurology, Leipzig, Germany

Rare Disease Specialist

Massachusetts General Hospital

Rare Disease Specialist

Children's Hospital of Philadelphia

Pediatrics, Pediatric Hematology-Oncology

New York Medical College

Pediatrics, Pediatric Hematology-Oncology

Masonic Cancer Center, University of Minnesota

Children's Hospital Medical Center, Cincinnati

Children's Hospital Medical Center, Cincinnati

Rare Disease Specialist

Jagiellonian University Medical College, Department of Neurology

Boston Children's Hospital

Great Ormond Street Hospital for Chidren NHS Foundation Trust

Hôpital Bicêtre

Pediatrics, Pediatric Critical Care Medicine

bluebird bio, Inc.

Institut du Cerveau et de la Moëlle épinière

Hugo W. Moser Research Institute at Kennedy Krieger, Inc.

Kremlin Bicêtre Hôpital

Beijing Tiantan Hospital, Capital Medical University, Beijing, China

Pediatrics, Pediatric Hematology-Oncology

University of Florida

Hugo W. Moser Research Institute at Kennedy Krieger, Inc.

University of Leipzig

Boston Children's Hospital

Medeos SRL

University of California, Los Angeles