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151 articles from the last 30 days matching "Research"

Clinical trialUNITERAREApr 3

New Recruiting Trial: MyPEEPS Mobile Plus: A Multi-Level HIV Prevention Intervention for Young MSM

Researchers at Columbia University are testing a new program called MyPEEPS Mobile Plus to help young men who have sex with men prevent HIV infection. The program uses multiple approaches, including mobile technology and community support, to reduce HIV risk. This trial is now accepting participants and will run through 2026.

WHY IT MATTERSThis trial is actively recruiting young MSM (men who have sex with men) ages 18-24 who want to learn evidence-based HIV prevention strategies through a mobile app and peer support program.
You can act on thisRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Culturally Adapting an Intervention to Increase Genetic Testing in African American Cancer Survivors

Researchers are looking for African American cancer survivors to join a study about genetic testing. The study will test a new approach designed specifically for African American communities to help more people get tested for inherited cancer genes. Genetic testing can show if someone has genes that increase cancer risk, which helps with prevention and treatment planning.

WHY IT MATTERSThis trial addresses a critical gap: African American cancer survivors are significantly underrepresented in genetic testing programs, meaning many miss opportunities for personalized cancer prevention and family screening.
You can act on thisRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Comparison of Molecular-Genetic Concordance of the Primary Tumor and Brain Metastases of Gastroesophageal Cancers

Researchers are looking for patients with gastroesophageal cancer (cancer of the food pipe and stomach) that has spread to the brain. This study will compare the genetic makeup of the original tumor with the cancer that spread to the brain to understand if they're the same or different. This information could help doctors choose better treatments for patients whose cancer has spread to the brain.

WHY IT MATTERSIf you have gastroesophageal cancer with brain metastases, this trial could help researchers understand why your cancer spread to the brain and potentially lead to more targeted treatment options in the future.
💬 Ask your doctorgastric canceresophageal cancergastroesophageal cancerRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: National Surveillance and Prevention of Neonatal VAP

Researchers at the University of Alberta are looking for participants for a study about preventing a serious lung infection called VAP (ventilator-associated pneumonia) in newborn babies. This infection happens when babies on breathing machines in the hospital develop pneumonia. The study will track cases across the country and test ways to stop this infection from happening.

WHY IT MATTERSIf your newborn is in a neonatal intensive care unit (NICU) on a ventilator, this trial could help identify prevention strategies that reduce the risk of developing a serious secondary infection during their hospital stay.
You can act on thisventilator-associated pneumoniaRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Evaluation of Xaluritamig in Adults, Adolescents and Children With Relapsed or Refractory Ewing Sarcoma (EWS)

Researchers are testing a new drug called Xaluritamig to treat Ewing sarcoma, a rare bone cancer that has come back or stopped responding to previous treatments. This is an early-stage study (Phase 1) that will include children, teenagers, and adults. The study is now accepting patients and is expected to start in April 2026.

WHY IT MATTERSThis trial offers a potential new treatment option for patients with relapsed or refractory Ewing sarcoma, a rare pediatric cancer with limited treatment alternatives after standard therapies fail.
You can act on thisEwing sarcomaRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Phase 3 Study of LUM-201 in Children With Growth Hormone Deficiency

Lumos Pharma is testing a new drug called LUM-201 in children who don't produce enough growth hormone naturally. This Phase 3 trial is the final stage of testing before the drug might be approved by the FDA. Researchers are actively recruiting children to participate and see if this treatment helps them grow taller.

WHY IT MATTERSThis is now actively recruiting children with growth hormone deficiency — families interested in potentially accessing LUM-201 before FDA approval should check eligibility requirements and contact the trial sites listed on ClinicalTrials.gov.
You can act on thisGrowth Hormone DeficiencyRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Assessing the Association Between H. Pylori Persistence and the Severity of Insulin Resistance in Patients With Metabolic Syndrome

Researchers are looking for people with metabolic syndrome (a group of conditions including high blood pressure, blood sugar, and cholesterol) to study whether a common stomach bacteria called H. pylori might make insulin resistance worse. Insulin resistance means your body has trouble using a hormone called insulin that controls blood sugar. The study will help doctors understand if treating this bacteria could help people with metabolic syndrome feel better.

WHY IT MATTERSIf H. pylori is found to worsen insulin resistance in metabolic syndrome patients, treating the infection could become a new way to help manage this common condition that affects millions of people.
💬 Ask your doctormetabolic syndromeRead →
ResearchPUBMEDApr 3

Artificial Intelligence, Connected Care, and Enabling Digital Health Technologies in Rare Diseases With a Focus on Lysosomal Storage Disorders: Scoping Review.

Researchers reviewed studies from the past 10 years about how artificial intelligence and connected care technologies can help patients with rare diseases, especially lysosomal storage disorders (LSDs)—conditions where the body can't break down certain substances properly. The review found that while these digital health tools show promise for helping doctors diagnose and manage these complex diseases, there are still big gaps in the research and not enough real-world examples of these technologies being used in patient care.

WHY IT MATTERSIf you have a lysosomal storage disorder, this research could lead to faster diagnosis, better remote monitoring through connected devices, and AI tools that help your doctors catch problems earlier—potentially improving your long-term care and quality of life.
Good to knowLysosomal Storage DisordersFabry diseaseGaucher diseaseRead →
ResearchPUBMEDApr 3

Systematic benchmarking demonstrates large language models have not reached the diagnostic accuracy of traditional rare-disease decision support tools.

Researchers tested whether artificial intelligence chatbots like ChatGPT could diagnose rare genetic diseases by comparing them to a traditional diagnostic tool called Exomiser. They tested seven different AI models on over 5,000 real patient cases. The study found that even the best AI chatbots were not as accurate as the existing diagnostic tool at identifying the correct disease.

WHY IT MATTERSIf you're waiting for a diagnosis for a rare genetic disease, this research shows that AI chatbots alone shouldn't replace traditional diagnostic tools—your doctor should continue using proven methods alongside any new technology.
Good to knowRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Immunotherapy (Nivolumab and Ipilimumab) With and Without a Live Biotherapeutic Product (EXL01) for the Treatment of Metastatic Renal Cell Cancer

Researchers are testing a new combination treatment for advanced kidney cancer that has spread to other parts of the body. The treatment combines two immunotherapy drugs (nivolumab and ipilimumab) with an experimental live biotherapeutic product called EXL01. This Phase 1 trial is now accepting patients to see if adding EXL01 to the standard immunotherapy improves outcomes.

WHY IT MATTERSThis trial offers metastatic renal cell carcinoma patients access to a novel combination approach that may enhance the effectiveness of existing immunotherapies by incorporating a live biotherapeutic product.
You can act on thismetastatic renal cell carcinomaRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Etoposide, Prednisone, Vincristine, Cyclophosphamide, and Doxorubicin (DA-EPOCH) With or Without Rituximab Plus Recombinant Erwinia Asparaginase (JZP458) for the Treatment of Newly Diagnosed Ph Negative B-Acute Lymphoblastic Leukemia or T Acute Lymphoblastic Leukemia

Researchers are looking for patients with a type of blood cancer called acute lymphoblastic leukemia (ALL) to test a new treatment combination. The study will test whether adding a drug called JZP458 to standard chemotherapy works better than chemotherapy alone. This trial is just starting and will recruit patients beginning in April 2026.

WHY IT MATTERSThis Phase 2 trial is now actively recruiting newly diagnosed ALL patients without the Philadelphia chromosome, offering access to an investigational asparaginase formulation (JZP458) that may have improved tolerability compared to standard asparaginase.
You can act on thisB-cell acute lymphoblastic leukemiaT-cell acute lymphoblastic leukemiaRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Exploratory Study of Umbilical Cord Blood-Derived CAR-NK Cell Therapy Targeting TRBC1/2 for Relapsed/Refractory T-Cell Lymphoma

Researchers are testing a new type of cell therapy made from umbilical cord blood to treat T-cell lymphoma that has stopped responding to other treatments. The therapy uses special immune cells called NK cells that are engineered to recognize and attack cancer cells. This is an early-stage study (Phase 1) that is now accepting patients.

WHY IT MATTERSThis trial offers a potential new treatment option for patients with relapsed or refractory T-cell lymphoma who have limited alternatives after standard therapies fail, with enrollment beginning in April 2026.
👁 Watch this spaceT-cell lymphomaRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Hepzato Kit and Opdualag for Metastatic Melanoma and Liver Metastasis

Researchers at the University of Wisconsin are testing a new combination of two cancer treatments called Hepzato Kit and Opdualag for patients with melanoma (a type of skin cancer) that has spread to the liver. This is an early-stage study that started in 2026 and is currently looking for patients to participate. The goal is to see if this combination can help people whose cancer has spread to multiple parts of their body.

WHY IT MATTERSThis trial offers patients with metastatic melanoma and liver involvement access to a novel combination therapy at a major academic medical center, potentially providing treatment options for a particularly aggressive cancer presentation.
You can act on thismetastatic melanomamelanoma with liver metastasisRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: A Study Investigating Intravenous Human Normal Immune Globulin (IGIV) 10% in Subjects With Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)

Researchers are testing a medicine called IGIV 10% to see if it helps people with CIDP, a rare nerve disease that causes weakness and numbness, usually in the legs and feet. IGIV is made from antibodies collected from donated blood. This is a Phase 3 trial, which means the medicine has already been tested in earlier studies and now doctors want to confirm it works well and is safe.

WHY IT MATTERSThis Phase 3 trial is now actively recruiting patients with CIDP — if you have confirmed CIDP diagnosis, you may be eligible to access a potential new treatment option before it becomes widely available.
You can act on thisChronic Inflammatory Demyelinating Polyneuropathy (CIDP)Read →
Clinical trialUNITERAREApr 3

New Recruiting Trial: A Study to Compare Elritercept With Epoetin Alfa to Treat Anemia in Adults With Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes (MDS) Who Need Regular Blood Transfusions

Researchers are testing a new drug called elritercept to see if it works better than a standard treatment (epoetin alfa) for anemia in adults with myelodysplastic syndromes (MDS)—a blood disorder where the bone marrow doesn't make enough healthy blood cells. People in this study have low, very low, or intermediate risk MDS and need regular blood transfusions. The trial is now accepting patients.

WHY IT MATTERSThis Phase 3 trial is actively recruiting adults with MDS who require transfusions, offering access to an investigational treatment that may reduce their dependence on blood transfusions.
You can act on thisMyelodysplastic SyndromesRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Prophylactic Transfusion In Pregnant in Women With Sickle Cell Disease

Researchers at Emory University are looking for pregnant women with sickle cell disease to join a study about blood transfusions. The study will test whether giving blood transfusions during pregnancy can help prevent serious complications for both the mother and baby. This is a Phase 4 trial, which means the treatment has already been tested before and researchers want to learn more about how well it works.

WHY IT MATTERSThis trial is now actively recruiting pregnant women with sickle cell disease — participation could help prevent pregnancy complications like stroke, organ damage, and miscarriage that occur at higher rates in this population.
You can act on thissickle cell diseaseRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Effects of Periodontal Treatment Associated With Antimicrobial Photodynamic Therapy on Halitosis in Patients With Diabetes Mellitus

Researchers are looking for people with diabetes to test a new way to treat bad breath caused by gum disease. The treatment combines regular gum cleaning with a special light therapy that kills bacteria in the mouth. This study will help doctors understand if this combination works better than standard gum treatment alone.

WHY IT MATTERSIf you have diabetes and struggle with bad breath despite good oral hygiene, this trial offers access to an innovative combination treatment that may address both the gum disease and halitosis that often accompany diabetes.
You can act on thisRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Skin Inflammation in Perimenopause: A Probiotic Intervention Proof of Concept Trial

Researchers at King's College London are testing whether probiotics (helpful bacteria) can reduce skin inflammation that some people experience during perimenopause (the years leading up to menopause). This is an early-stage study to see if this approach might work before larger trials are done. The study is now accepting participants.

WHY IT MATTERSIf probiotics prove effective for perimenopause-related skin inflammation, this could offer a non-hormonal treatment option for people experiencing this symptom during the menopausal transition.
👁 Watch this spaceRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Exploration of Systemic and Portal Hemostasis in Patients Undergoing Transjugular Intrahepatic Portosystemic Shunt Placement

Researchers are looking for patients who need a procedure called a transjugular intrahepatic portosystemic shunt (TIPS) to help study how blood clotting works in patients with liver disease. This trial will examine blood clotting patterns before and after the procedure to better understand how TIPS affects the body's ability to form and break down blood clots. The study is recruiting patients starting in April 2026 and is being run by hospitals in Paris.

WHY IT MATTERSThis trial is now recruiting patients undergoing TIPS placement — if you have advanced liver disease with portal hypertension and are scheduled for this procedure, you may be eligible to contribute to research that could improve how doctors manage bleeding risks in liver disease patients.
💬 Ask your doctorportal hypertensionadvanced liver diseasecirrhosisRead →
Clinical trialUNITERAREApr 3

New Recruiting Trial: Transcranial Direct Current Stimulation in Children With Autism

Researchers at New York State Institute for Basic Research are testing a new treatment called transcranial direct current stimulation (tDCS) in children with autism. This treatment uses mild electrical currents applied to the scalp to potentially help with autism symptoms. The study is now accepting children to participate and will begin in April 2026.

WHY IT MATTERSThis trial offers families with autistic children a chance to explore a non-medication brain stimulation approach that may help with core autism symptoms, with enrollment actively opening at a major research institution.
👁 Watch this spaceAutism Spectrum DisorderRead →
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