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2 articles from the last 90 days matching "Humans"

PolicyRSSApr 3

FDA Releases Draft Guidance on Alternatives to Animal Testing in Drug Development

The FDA released new guidelines to help drug companies test medicines using human-based methods instead of animal testing. These new testing approaches could make it faster and safer to develop drugs by using data that better reflects how humans respond. This is part of the FDA's effort to bring effective treatments to patients more quickly.

WHY IT MATTERSPatients with rare diseases could gain access to new treatments faster if drug developers can use these human-centered testing methods instead of spending years on animal studies.
ℹ Good to knowRead →
Clinical trialCLINICALTRIALSMar 26

Trial Now Recruiting: A Study of SGT-212 Gene Therapy in Friedreich's Ataxia (NCT07180355)

Researchers are testing a new gene therapy called SGT-212 for Friedreich's ataxia, a rare disease that affects how the body moves and coordinates. This is the first time this treatment is being tested in humans. The study will enroll 10 patients and follow them for about 5 years to see if the treatment is safe and works well.

WHY IT MATTERSThis is the first human trial of SGT-212 for Friedreich's ataxia, offering eligible patients access to a potentially disease-modifying gene therapy that addresses the underlying genetic cause rather than just managing symptoms.
→ You can act on thisFriedreich's AtaxiaRead →

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