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1 article from the last 30 days matching "Frontotemporal dementia with motor neuron disease"

Clinical trialRSSToday

RAG-17 shows promise in SOD1-ALS trial, reducing damage markers

Scientists are testing a new drug called RAG-17 for people with a specific type of ALS (a disease that weakens muscles over time) caused by a SOD1 gene mutation. Early results show the drug was safe at different doses and made important disease markers improve. This is early-stage testing, but it's a promising first step.

WHY IT MATTERSIf you have SOD1-ALS, this is one of the first treatments specifically designed for your genetic form of the disease, and early signs suggest it may slow the damage happening in your body.
💬 Ask your doctoramyotrophic lateral sclerosis (SOD1-ALS)Read →

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