Rare disease news

FDA approvals, research breakthroughs, clinical trials, and advocacy updates

Curated and summarized by AI for patients and caregivers

🔍
AllDrug approvalsClinical trialsResearchGrants & fundingAdvocacy & policyPipeline
Show:All newsBreaking onlyImportant & breaking
Date:7 days30 days90 daysAll time

1 article matching "targeted treatment"

Clinical trialCLINICALTRIALSMar 26

Trial Results Posted: Testing AZD9291 as Potentially Targeted Treatment in Cancers With EGFR Genetic Changes (MATCH-Subprotocol E) (NCT06303167)

Researchers tested a cancer drug called osimertinib (AZD9291) in 19 patients with advanced cancers that have specific genetic changes in a gene called EGFR. The drug works by blocking a mutated protein that helps cancer cells grow. This trial is now complete and results have been posted.

WHY IT MATTERSThis trial provides evidence that osimertinib may work against cancers with EGFR mutations across different cancer types, potentially offering a treatment option for patients whose tumors have this specific genetic change.
💬 Ask your doctorAdvanced LymphomaAdvanced Malignant Solid NeoplasmRefractory Lymphoma

Get personalized rare disease news

Follow your conditions to see news about the diseases that matter to you — FDA approvals, trial openings, and research breakthroughs.

Create free account →Browse diseases