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NewsBLOODMonday, October 20, 2025 · October 20, 2025

Hemophilia A Gene Therapy Shows Durable Response at 3 Years

WHY IT MATTERS

Gene therapy may offer functional cure for severe hemophilia A.

Three-year follow-up data for valoctocogene roxaparvovec shows sustained factor VIII expression and significant reduction in bleeding events.

Read the original at Blood
ResearchGene Therapy

Related conditions

Hemophilia A