How 19 Points Changed My Grandson’s DMD Journey
WHY IT MATTERS
If your child with DMD has been told they don't qualify for a trial, this story shows that eligibility criteria can sometimes be reconsidered or adjusted—it's worth asking your doctor whether similar flexibility might apply to your situation.
A grandmother shares how a small change in how her grandson's condition was measured helped him qualify for a Duchenne muscular dystrophy (DMD) treatment trial. Researchers adjusted the scoring system by 19 points, which gave him a second chance to participate in the study. This story highlights how trial eligibility rules can sometimes be adjusted to help more patients access new treatments.
A grandmother explains how researchers gave her grandson a second chance at qualifying for a Duchenne muscular dystrophy (DMD) trial. The post How 19 Points Changed My Grandson’s DMD Journey appeared first on Rare Disease Advisor
ASK YOUR DOCTOR
Ask your DMD specialist whether there are any active trials your family member might qualify for, and whether eligibility criteria have any flexibility or alternative assessment methods.