Trial Completed: Natural History Study of Patients With Canavan Disease (CANinform Study) (NCT04126005)
WHY IT MATTERS
This completed natural history study provides detailed data on how Canavan disease progresses in children, which is essential for designing future clinical trials and understanding what to expect from the disease.
Researchers completed a study that collected information about how Canavan disease develops and progresses in children. The study looked at medical records from 67 patients and also gathered new information about their movement abilities and important health milestones. This type of study helps doctors understand the disease better and can guide future treatment development.
NCT ID: NCT04126005 Status: COMPLETED Conditions: Canavan Disease Enrollment: 67 Sponsor: Aspa Therapeutics Summary: This study uses medical records that allow retrospective data extraction of critical milestone and motor function data. In addition, prospective assessments collect data relevant to the natural history of Canavan disease in children.