Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

5 matching diseasesClear search ×

Syndromic orbital border hypoplasia

Urrets-Zavalia syndrome

ORPHA:98606

Lethal ataxia with deafness and optic atrophy

Arts syndrome · Lethal ataxia with hearing loss and optic atrophy

ORPHA:1187

Müllerian derivatives-lymphangiectasia-polydactyly syndrome

Urioste syndrome

ORPHA:1655

Rett syndrome

ORPHA:778

ZTTK syndrome

Zhu-Tokita-Takenouchi-Kim syndrome · Facial dysmorphism-brain malformations-musculoskeletal abnormalities-intellectual disability syndrome

ORPHA:500150