Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

3 matching diseasesClear search ×

SIM1-related Prader-Willi-like syndrome

SIM1-related PWLS

ORPHA:398079

MGP-related spondyloepiphyseal dysplasia

MGP-related SED · Spondyloepiphyseal dysplasia-platyspondyly-brachytelephalangism syndrome

ORPHA:664377

SIX2-related frontonasal dysplasia

SIX2-related FND

ORPHA:488437