Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

4 matching diseasesClear search ×

Potassium-aggravated myotonia

K+-aggravated myotonia · K-aggravated myotonia

ORPHA:612

Hyperzincemia and hypercalprotectinemia

PSTPIP1-associated myeloid-related proteinemia inflammatory syndrome · PAMI syndrome

ORPHA:251523

Brain dopamine-serotonin vesicular transport disease

ORPHA:352649

Dopamine beta-hydroxylase deficiency

DBH deficiency

ORPHA:230