Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

5 matching diseasesClear search ×

OBSOLETE: Inherited predisposition to essential thrombocythemia

OBSOLETE: Familial essential thrombocythemia

ORPHA:225968

Essential thrombocythemia

ET · Essential thrombocytosis

ORPHA:3318

Familial thrombocytosis

Familial thrombocythemia · Hereditary thrombocythemia

ORPHA:71493

OBSOLETE: Familial cervical artery dissection

OBSOLETE: Familial CAD · OBSOLETE: Hereditary CAD

ORPHA:36382

OBSOLETE: Familial esophageal achalasia

ORPHA:99723