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Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.
Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"
Metachromatic leukodystrophy
Arylsulfatase A deficiency · MLD
Metachromatic leukodystrophy, adult form
Arylsulfatase A deficiency, adult form · MLD, adult form
Metachromatic leukodystrophy, juvenile form
Arylsulfatase A deficiency, juvenile form · MLD, juvenile form
Metachromatic leukodystrophy, late infantile form
Arylsulfatase A deficiency, late infantile form · MLD, late infantile form