Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

6 matching diseasesClear search ×

Rippling muscle disease with myasthenia gravis

Acquired rippling muscle disease · Generalized myasthenia gravis

ORPHA:206575

IgG4-related disease

IgG4-related sclerosing disease · Immunoglobulin G4-related sclerosing disease

ORPHA:284264

Immune-mediated acquired neuromuscular junction disease

ORPHA:464764

Immune-mediated scleritis

ORPHA:648681

Rare immune disease

ORPHA:98004

Rippling muscle disease

ORPHA:97238