Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

6 matching diseasesClear search ×

Infant acute respiratory distress syndrome

Hyaline membrane disease · Infant ARDS

ORPHA:70587

Neonatal acute respiratory distress syndrome

Neonatal RDS · Hyaline membrane disease

ORPHA:217563

Anti-glomerular basement membrane disease

Anti-GBM syndrome

ORPHA:375

Erythema palmare hereditarium

Lane disease · Red palms disease

ORPHA:231031

Meige disease

Hereditary lymphedema type II · Meige lymphedema

ORPHA:90186

OBSOLETE: Basement membrane disease

ORPHA:93550