Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

5 matching diseasesClear search ×

Pelviscapular dysplasia

Cousin syndrome · Familial pelvis-scapular dysplasia

ORPHA:93333

DICER1 tumor-predisposition syndrome

PPBFTDS · Pleuropulmonary blastoma familial tumor and dysplasia syndrome

ORPHA:284343

Focal facial dermal dysplasia type IV

FFDD type IV · FFDD4

ORPHA:398189

Hip dysplasia, Beukes type

BFHD · Beukes familial hip dysplasia

ORPHA:2114

Pelvis-shoulder dysplasia

Kosenow syndrome · Scapuloiliac dysostosis

ORPHA:2839