Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

6 matching diseasesClear search ×

Familial isolated café-au-lait macules

Familial isolated CALSs · Multiple isolated café-au-lait spots

ORPHA:2678

Familial isolated congenital asplenia

ORPHA:101351

Familial isolated dilated cardiomyopathy

Familial or idiopathic dilated cardiomyopathy

ORPHA:154

Familial isolated pituitary adenoma

FIPA

ORPHA:314777

Familial isolated trichomegaly

ORPHA:411788

Isolated familial medullary thyroid carcinoma

Hereditary isolated MTC · Isolated familial MTC

ORPHA:99361