Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

7 matching diseasesClear search ×

Diamond-Blackfan anemia

Diamond-Blackfan anemia syndrome · Congenital PRCA

ORPHA:124

ANE syndrome

Alopecia-progressive neurological defect-endocrinopathy syndrome

ORPHA:157954

Autoerythrocyte sensitization syndrome

GDS · Gardner-Diamond syndrome

ORPHA:324636

Blue diaper syndrome

Drummond syndrome · Familial hypercalcemia-nephrocalcinosis-indicanuria syndrome

ORPHA:94086

Brachydactyly-nystagmus-cerebellar ataxia syndrome

Biemond syndrome

ORPHA:1246

Ghosal hematodiaphyseal dysplasia

Diaphyseal dysplasia-anemia syndrome · Ghosal syndrome

ORPHA:1802

Shwachman-Diamond syndrome

Pancreatic insufficiency and bone marrow dysfunction · SDS

ORPHA:811