Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

4 matching diseasesClear search ×

DITRA

Deficiency of IL-36R antagonist · Deficiency of IL-36Ra

ORPHA:404546

Apolipoprotein A-I deficiency

ApoA-I deficiency · Familial apoA-I deficiency

ORPHA:425

Pyridoxine-dependent-developmental and epileptic encephalopathy

Antiquitin deficiency · Vitamin B6-dependent seizures

ORPHA:3006

Sterile multifocal osteomyelitis with periostitis and pustulosis

Autoinflammatory disease due to interleukin-1 receptor antagonist deficiency · DIRA

ORPHA:210115