Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

6 matching diseasesClear search ×

Congenital lobar emphysema

Congenital lobar hyperinflation · Infantile lobar hyperinflation

ORPHA:1928

Congenital central hypoventilation syndrome

CCHS · Ondine syndrome

ORPHA:661

Congenital Epstein-Barr virus infection

Antenatal Epstein-Barr virus infection · Mother-to-child transmission of Epstein-Barr virus infection

ORPHA:70596

Congenital isolated hyperinsulinism

PHHI · Persistent hyperinsulinemic hypoglycemia of infancy

ORPHA:657

Congenital limb malformation

ORPHA:68378

Congenital peritoneal encapsulation

CPE · Peritoneal encapsulation syndrome

ORPHA:697986