Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

4 matching diseasesClear search ×

Allan-Herndon-Dudley syndrome

AHDS · MCT8 deficiency

ORPHA:59

Neurodegenerative syndrome due to cerebral folate transport deficiency

Folate receptor alpha deficiency · Cerebral folate transport deficiency

ORPHA:217382

Riboflavin transporter deficiency

Brown-Vialetto-van Laere syndrome

ORPHA:97229

X-linked creatine transporter deficiency

Creatine transporter deficiency · SLC6A8 deficiency

ORPHA:52503