Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

4 matching diseasesClear search ×

Microcephaly-albinism-digital anomalies syndrome

Castro Gago-Pombo-Novo syndrome

ORPHA:2513

Opsoclonus-myoclonus syndrome

Ataxo-opso-myoclonus syndrome · Dancing eye syndrome

ORPHA:1183

Port-wine nevi-mega cisterna magna-hydrocephalus syndrome

Nova syndrome

ORPHA:2703

Rombo syndrome

ORPHA:3110