Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

4 matching diseasesClear search ×

Hip dysplasia, Beukes type

BFHD · Beukes familial hip dysplasia

ORPHA:2114

DICER1 tumor-predisposition syndrome

PPBFTDS · Pleuropulmonary blastoma familial tumor and dysplasia syndrome

ORPHA:284343

Familial developmental dysphasia

Billard-Toutain-Maheut syndrome · FOXP2-associated dysphasia

ORPHA:1799

Pelviscapular dysplasia

Cousin syndrome · Familial pelvis-scapular dysplasia

ORPHA:93333