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7 Patents Filed · HIPAA-Aligned · Free for Patients · Westwood, MA
Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.
Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"
Autosomal recessive axonal neuropathy with neuromyotonia
ARAN-NM · ARCMT2-NM
Autosomal recessive axonal hereditary motor and sensory neuropathy
AR-CMT2 · Autosomal recessive axonal Charcot-Marie-Tooth disease type 2
Autosomal recessive Charcot-Marie-Tooth disease type 2X
CMT2X · Autosomal recessive Charcot-Marie-Tooth disease type 2 due to SPG11 mutation
Autosomal recessive Charcot-Marie-Tooth disease with hoarseness
ARCMT2K · Autosomal recessive axonal CMT4C4