Overview
FDA & Trial Timeline
5 eventsNational Heart, Lung, and Blood Institute (NHLBI) — NA
Swedish Orphan Biovitrum — PHASE2
Washington University School of Medicine — PHASE1
Gruppo Italiano Malattie EMatologiche dell'Adulto
Technische Universität Dresden
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
No FDA-approved treatments are currently listed for VEXAS syndrome.
5 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.
View clinical trials →Rare Disease Specialist
Rare Disease Specialist
Treatment Centers
8 centersNational Institutes of Health Clinical Center
📍 Bethesda, Maryland
👤 Payal P Khincha, M.D.
👤 Christopher Grunseich, M.D.
Washington University School of Medicine
📍 St Louis, Missouri
👤 Meagan A Jacoby, M.D., Ph.D.
👤 Janssen Research & Development, LLC Clinical Trial
Dana Farber Cancer Institute
📍 Boston, Massachusetts
👤 Janssen Research & Development, LLC Clinical Trial
Fred Hutchinson Cancer Center
📍 Seattle, Washington
👤 Sawa M Ito, MD, PhD
Baylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
Travel Grants
No travel grants are currently matched to VEXAS syndrome.
Community
No community posts yet. Be the first to share your experience with VEXAS syndrome.
Start the conversation →Latest news about VEXAS syndrome
Disease timeline:
New recruiting trial: HRQoL and Financial Toxicity in Patients With VEXAS Syndrome
A new clinical trial is recruiting patients for VEXAS syndrome
New recruiting trial: Multicenter, Interdisciplinary National VEXAS Registry With Accompanying Biomaterial Collection
A new clinical trial is recruiting patients for VEXAS syndrome
New trial: Molecular and Clinical Analysis of Bone Marrow Failure: A Secondary Research Study
Phase NA trial recruiting.
New trial: Pacritinib in Vacuoles, E1 Ubiqutin-activating Enzyme, X-linked, Autoinflammatory, Somatic (VEXAS) S
Phase PHASE1 trial recruiting. Pacritinib
New trial: A Study to Assess the Effectiveness and Safety of Pacritinib in Patients With VEXAS Syndrome (PAXIS)
Phase PHASE2 trial recruiting. Pacritinib
Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about VEXAS syndrome
Are there clinical trials for VEXAS syndrome?
Yes — 5 recruiting clinical trials are currently listed for VEXAS syndrome on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.
Which specialists treat VEXAS syndrome?
7 specialists and care centers treating VEXAS syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.