Velo-facial-skeletal syndrome

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ORPHA:3424OMIM:600736Q87.0
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Overview

Velo-facial-skeletal syndrome, also sometimes referred to as Velo-facial-skeletal dysplasia, is an extremely rare genetic condition that affects multiple body systems, particularly the palate (the roof of the mouth), the face, and the skeleton. The name reflects the three main areas involved: 'velo' refers to the soft palate (velum), 'facial' refers to distinctive facial features, and 'skeletal' refers to bone and joint abnormalities. People with this condition may have a cleft palate or a high-arched palate, unusual facial features such as a flat midface, a small jaw, or widely spaced eyes, and various skeletal problems including short stature, joint looseness, and abnormalities of the spine or limbs. Some individuals may also experience speech difficulties related to palate problems, hearing issues, and mild developmental delays. Because this syndrome is so rare, there is no specific cure. Treatment focuses on managing individual symptoms. This may include surgery to repair a cleft palate, speech therapy, orthopedic care for skeletal problems, and regular monitoring by a team of specialists. Early intervention and coordinated care can significantly improve quality of life for affected individuals.

Key symptoms:

Cleft palate or high-arched palateDistinctive facial featuresShort statureSmall jaw (micrognathia)Loose or overly flexible jointsFlat midfaceWidely spaced eyesSpine abnormalitiesLimb or bone abnormalitiesSpeech difficultiesHearing problemsFeeding difficulties in infancyMild developmental delays

Clinical phenotype terms (18)— hover any for plain English
Prominent fingertip padsHP:0001212
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Velo-facial-skeletal syndrome.

View clinical trials →

No actively recruiting trials found for Velo-facial-skeletal syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Velo-facial-skeletal syndrome community →

No specialists are currently listed for Velo-facial-skeletal syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Velo-facial-skeletal syndrome.

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Community

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Latest news about Velo-facial-skeletal syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific features of this syndrome does my child have, and how severe are they?,When should cleft palate repair surgery be done, and what can we expect from recovery?,What genetic testing would you recommend for our family?,How often should my child have hearing and vision screenings?,What therapies (speech, physical, occupational) should we start, and when?,Are there any skeletal problems we need to monitor as my child grows?,Can you connect us with other families or support groups for rare craniofacial or skeletal conditions?

Common questions about Velo-facial-skeletal syndrome

What is Velo-facial-skeletal syndrome?

Velo-facial-skeletal syndrome, also sometimes referred to as Velo-facial-skeletal dysplasia, is an extremely rare genetic condition that affects multiple body systems, particularly the palate (the roof of the mouth), the face, and the skeleton. The name reflects the three main areas involved: 'velo' refers to the soft palate (velum), 'facial' refers to distinctive facial features, and 'skeletal' refers to bone and joint abnormalities. People with this condition may have a cleft palate or a high-arched palate, unusual facial features such as a flat midface, a small jaw, or widely spaced eyes,

How is Velo-facial-skeletal syndrome inherited?

Velo-facial-skeletal syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Velo-facial-skeletal syndrome typically begin?

Typical onset of Velo-facial-skeletal syndrome is neonatal. Age of onset can vary across affected individuals.