Undifferentiated carcinoma of liver and intrahepatic biliary tract

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:424970C22.0
Who is this for?
Show terms as
1FDA treatments8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Undifferentiated carcinoma of the liver and intrahepatic biliary tract is a very rare and aggressive form of liver cancer. Unlike more common liver cancers such as hepatocellular carcinoma (HCC) or cholangiocarcinoma, this tumor is called 'undifferentiated' because the cancer cells look so abnormal under a microscope that doctors cannot tell which type of liver or bile duct cell they originally came from. It may also be referred to as undifferentiated liver carcinoma or undifferentiated hepatic carcinoma. This cancer grows in the liver or in the bile ducts located inside the liver (called intrahepatic bile ducts). Because it is undifferentiated, it tends to grow and spread quickly. The liver plays a vital role in filtering blood, producing proteins, and helping with digestion, so when cancer disrupts these functions, patients can feel very unwell. Symptoms often include abdominal pain, unexplained weight loss, and yellowing of the skin. Treatment is very challenging because this cancer type is rare and does not always respond well to standard therapies. Surgery to remove the tumor, when possible, is the main treatment approach. Chemotherapy and other systemic therapies may be used, but outcomes are often poor. Research into better treatments is ongoing, and patients are encouraged to seek care at specialized cancer centers.

Also known as:

Key symptoms:

Pain or discomfort in the upper right side of the abdomenUnexplained weight lossLoss of appetiteYellowing of the skin and whites of the eyes (jaundice)Swelling or bloating of the abdomenExtreme tiredness and fatigueNausea or vomitingDark-colored urinePale or clay-colored stoolsFever without a clear causeFeeling full quickly after eating

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Adult

Begins in adulthood (age 18 or older)

Orphanet ↗NORD ↗

FDA & Trial Timeline

1 event
Sep 2021

CABOMETYX: FDA approved

Treatment of adult and pediatric patients 12 years of age and older with locally advanced or metastatic differentiated thyroid cancer (DTC) that has progressed following prior VEGFR-targeted therapy and who are radioactive iodine-refractory or ineligible

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

CABOMETYX

cabozantinib· Exelixis, Inc.Orphan Drug
Treatment of adult and pediatric patients 12 years of age and older with locally advanced or metastatic differentiated thyroid cancer (DTC) that has progressed following prior VEGFR-targeted therapy a

Treatment of adult and pediatric patients 12 years of age and older with locally advanced or metastatic differentiated thyroid cancer (DTC) that has progressed following prior VEGFR-targeted therapy and who are radioactive iodine-refractory or ineligible

No actively recruiting trials found for Undifferentiated carcinoma of liver and intrahepatic biliary tract at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Undifferentiated carcinoma of liver and intrahepatic biliary tract community →

No specialists are currently listed for Undifferentiated carcinoma of liver and intrahepatic biliary tract.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Undifferentiated carcinoma of liver and intrahepatic biliary tract.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Undifferentiated carcinoma of liver and intrahepatic biliary tractForum →

No community posts yet. Be the first to share your experience with Undifferentiated carcinoma of liver and intrahepatic biliary tract.

Start the conversation →

Latest news about Undifferentiated carcinoma of liver and intrahepatic biliary tract

No recent news articles for Undifferentiated carcinoma of liver and intrahepatic biliary tract.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Has the cancer spread beyond the liver, and what does that mean for my treatment options?,Is surgery or liver transplantation an option for me, and what are the risks?,Should my tumor tissue be tested for specific genetic mutations that might guide treatment?,Are there any clinical trials I might be eligible for?,What are the realistic goals of treatment — cure, controlling the cancer, or managing symptoms?,What support services, such as palliative care or nutrition counseling, are available to me?,Should my family members be tested for any hereditary cancer syndromes?

Common questions about Undifferentiated carcinoma of liver and intrahepatic biliary tract

What is Undifferentiated carcinoma of liver and intrahepatic biliary tract?

Undifferentiated carcinoma of the liver and intrahepatic biliary tract is a very rare and aggressive form of liver cancer. Unlike more common liver cancers such as hepatocellular carcinoma (HCC) or cholangiocarcinoma, this tumor is called 'undifferentiated' because the cancer cells look so abnormal under a microscope that doctors cannot tell which type of liver or bile duct cell they originally came from. It may also be referred to as undifferentiated liver carcinoma or undifferentiated hepatic carcinoma. This cancer grows in the liver or in the bile ducts located inside the liver (called int

How is Undifferentiated carcinoma of liver and intrahepatic biliary tract inherited?

Undifferentiated carcinoma of liver and intrahepatic biliary tract follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Undifferentiated carcinoma of liver and intrahepatic biliary tract typically begin?

Typical onset of Undifferentiated carcinoma of liver and intrahepatic biliary tract is adult. Age of onset can vary across affected individuals.