Overview
Tyrosinemia is treated with 4 medications in our database, including ORFADIN, NITYR, Nitisinone, Orfadin. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Swedish Orphan Biovitrum AB (publ), Cycle, Swedish Orphan Biovitrum. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Tyrosinemia treatment below.
Autosomal recessive
Passed on when both parents carry the same gene change; often skips generations
Variable
Can begin at different ages, from infancy through adulthood
Treatments
3 availableNITYR
* Patient Copay Amount: $0 co-pay for eligible patients * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Benefits may be limited to commercially insured patients
ORFADIN
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi
Nitisinone
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi
Clinical Trials
View all trials with filters →No actively recruiting trials found for Tyrosinemia at this time.
New trials open frequently. Follow this disease to get notified.
Rare Disease Specialist
Rare Disease Specialist
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Travel Grants
No travel grants are currently matched to Tyrosinemia.
Community
No community posts yet. Be the first to share your experience with Tyrosinemia.
Start the conversation →Latest news about Tyrosinemia
No recent news articles for Tyrosinemia.
Follow this condition to be notified when news becomes available.
Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Tyrosinemia
What is Tyrosinemia?
Tyrosinemia is treated with 4 medications in our database, including ORFADIN, NITYR, Nitisinone, Orfadin. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Swedish Orphan Biovitrum AB (publ), Cycle, Swedish Orphan Biovitrum. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Tyrosinemia treatment below.
How is Tyrosinemia inherited?
Tyrosinemia follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.
Which specialists treat Tyrosinemia?
4 specialists and care centers treating Tyrosinemia are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.
What treatment and support options exist for Tyrosinemia?
3 FDA-approved treatments are currently tracked on UniteRare for Tyrosinemia. See the treatments and support programs sections for copay assistance, eligibility, and contact details.