Syndromic recessive X-linked ichthyosis

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ORPHA:281090OMIM:308100Q80.1
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Overview

Syndromic recessive X-linked ichthyosis is a rare genetic skin condition that belongs to a group of disorders called ichthyoses, which cause dry, scaly skin. Unlike the more common non-syndromic form of X-linked ichthyosis (which mainly affects the skin), the syndromic form involves additional body systems beyond the skin. This condition is caused by a larger deletion on the X chromosome that removes the STS gene (steroid sulfatase) along with neighboring genes. Because of these larger deletions, affected individuals may experience not only the characteristic dark, plate-like scales on the skin but also additional features such as intellectual disability, epilepsy, attention deficit hyperactivity disorder (ADHD), and sometimes abnormalities of the eyes (corneal opacities) or undescended testes. The specific combination of extra features depends on which neighboring genes are also deleted. Since it is X-linked recessive, it primarily affects males, while females who carry one copy of the deletion are usually unaffected or only mildly affected. Treatment is mainly supportive and focuses on managing the skin symptoms with moisturizers and keratolytic creams, while the additional features require care from multiple specialists. There is currently no cure, but early diagnosis and coordinated care can significantly improve quality of life.

Also known as:

Key symptoms:

Dark, thick, plate-like scales on the skinDry skin that worsens in cold or dry weatherScaling that often spares the palms and solesIntellectual disability (ranging from mild to moderate)Seizures or epilepsyAttention deficit hyperactivity disorder (ADHD)Behavioral difficultiesUndescended testes (cryptorchidism) in boysCloudy spots on the cornea of the eyeShort stature in some casesDelayed developmental milestonesHypogonadism (low hormone levels from the testes)Bone abnormalities in some cases (such as chondrodysplasia punctata)

Clinical phenotype terms (21)— hover any for plain English
LissencephalyHP:0001339Acute leukemiaHP:0002488Abnormal stomach morphologyHP:0002577Abnormal abdominal wall morphologyHP:0004298Abdominal wall defectHP:0010866Testicular seminomaHP:0100617
Inheritance

X-linked recessive

Carried on the X chromosome; typically affects males more than females

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Syndromic recessive X-linked ichthyosis.

View clinical trials →

No actively recruiting trials found for Syndromic recessive X-linked ichthyosis at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Syndromic recessive X-linked ichthyosis community →

No specialists are currently listed for Syndromic recessive X-linked ichthyosis.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Syndromic recessive X-linked ichthyosis.

Search all travel grants →NORD Financial Assistance ↗

Community

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Caregiver Resources

NORD Caregiver Resources

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Mental Health Support

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Family & Caregiver Grants

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Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How large is the deletion on my child's X chromosome, and which genes are affected?,What additional health problems should we watch for based on the specific deletion?,What is the best daily skin care routine for managing the ichthyosis?,Should my child be evaluated by a neurologist or developmental specialist?,Are there any clinical trials or new treatments being studied for this condition?,What are the chances of this condition occurring in future pregnancies?,What school accommodations or therapies should we consider for my child?

Common questions about Syndromic recessive X-linked ichthyosis

What is Syndromic recessive X-linked ichthyosis?

Syndromic recessive X-linked ichthyosis is a rare genetic skin condition that belongs to a group of disorders called ichthyoses, which cause dry, scaly skin. Unlike the more common non-syndromic form of X-linked ichthyosis (which mainly affects the skin), the syndromic form involves additional body systems beyond the skin. This condition is caused by a larger deletion on the X chromosome that removes the STS gene (steroid sulfatase) along with neighboring genes. Because of these larger deletions, affected individuals may experience not only the characteristic dark, plate-like scales on the ski

How is Syndromic recessive X-linked ichthyosis inherited?

Syndromic recessive X-linked ichthyosis follows a x-linked recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Syndromic recessive X-linked ichthyosis typically begin?

Typical onset of Syndromic recessive X-linked ichthyosis is neonatal. Age of onset can vary across affected individuals.