Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:431320
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Spastic paraplegia-optic atrophy-neuropathy syndrome, sometimes called SPOAN syndrome, is a rare inherited neurological disease that affects the nervous system in several ways at the same time. The name describes its three main features: spastic paraplegia (stiffness and weakness in the legs), optic atrophy (damage to the nerve that carries vision signals from the eye to the brain), and neuropathy (damage to the nerves outside the brain and spinal cord, affecting sensation and movement in the limbs). Together, these problems make it hard to walk, see clearly, and feel normal sensations in the hands and feet. The disease is caused by changes (mutations) in the KIF1C gene, which gives instructions for a protein that helps move important materials inside nerve cells. When this protein does not work properly, nerve cells gradually stop functioning as they should. Symptoms usually begin in childhood or early adulthood and tend to get worse over time. People with this condition may also experience muscle wasting, difficulty with coordination, and in some cases mild intellectual challenges. There is currently no cure for this condition. Treatment focuses on managing symptoms, keeping people as mobile and comfortable as possible, and supporting quality of life. Physical therapy, assistive devices, and regular monitoring by a team of specialists are the main approaches used today.

Also known as:

Key symptoms:

Stiffness and weakness in the legs (spastic paraplegia)Gradual loss of vision due to optic nerve damage (optic atrophy)Numbness, tingling, or weakness in the hands and feet (peripheral neuropathy)Difficulty walking or loss of ability to walk over timeMuscle wasting, especially in the legs and feetPoor coordination and balance problemsReduced or absent reflexes in the legsSensitivity to pain or temperature may be reducedMild intellectual disability in some individualsBladder control problems in some cases

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder.

View clinical trials →

No actively recruiting trials found for Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder community →

No specialists are currently listed for Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorderForum →

No community posts yet. Be the first to share your experience with Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder.

Start the conversation →

Latest news about Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder

No recent news articles for Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which specific mutation in the KIF1C gene does my family member have, and what does that mean for how the disease will progress?,Should other family members, including siblings and parents, be tested for this condition?,What therapies or assistive devices would you recommend right now to help maintain mobility as long as possible?,Are there any clinical trials or research studies we could participate in?,How often should vision be checked, and is there anything that can slow the vision loss?,What signs of worsening should prompt us to seek urgent medical attention?,Are there patient registries or support groups for families affected by SPOAN syndrome or hereditary spastic paraplegia?

Common questions about Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder

What is Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder?

Spastic paraplegia-optic atrophy-neuropathy syndrome, sometimes called SPOAN syndrome, is a rare inherited neurological disease that affects the nervous system in several ways at the same time. The name describes its three main features: spastic paraplegia (stiffness and weakness in the legs), optic atrophy (damage to the nerve that carries vision signals from the eye to the brain), and neuropathy (damage to the nerves outside the brain and spinal cord, affecting sensation and movement in the limbs). Together, these problems make it hard to walk, see clearly, and feel normal sensations in the

How is Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder inherited?

Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder typically begin?

Typical onset of Spastic paraplegia-optic atrophy-neuropathy and spastic paraplegia-optic atrophy-neuropathy-related disorder is childhood. Age of onset can vary across affected individuals.