Spastic paraparesis-deafness syndrome

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ORPHA:2815OMIM:312910G11.4
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8Treatment centers

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Overview

Spastic paraparesis-deafness syndrome is an extremely rare inherited neurological condition that combines progressive stiffness and weakness in the legs (spastic paraparesis) with hearing loss (deafness or sensorineural hearing impairment). The disease affects the nervous system in two main ways: it damages the nerve pathways that control leg movement, leading to increasing difficulty with walking and leg stiffness, and it impairs the nerves or structures involved in hearing. Patients typically notice gradual stiffening of the legs, trouble walking, and progressive hearing loss that may begin in childhood or later in life. Because this syndrome is so rare, only a small number of families have been described in the medical literature. The exact genetic cause has not been fully established in all reported cases, and the condition may be genetically heterogeneous, meaning different genetic changes in different families can cause a similar set of symptoms. There is currently no cure for this condition. Treatment focuses on managing symptoms, including physical therapy and rehabilitation to maintain mobility, medications to reduce muscle spasticity (such as baclofen or tizanidine), and hearing aids or cochlear implants to address hearing loss. A multidisciplinary team of specialists is typically needed to provide the best care.

Also known as:

Key symptoms:

Progressive leg stiffness (spasticity)Difficulty walkingWeakness in the legsHearing loss that worsens over timeAbnormal gait or walking patternIncreased muscle tone in the lower limbsExaggerated reflexes in the legsBalance problemsFoot deformities such as high arches or curled toesBladder control difficultiesFatigue in the legs after walking

Clinical phenotype terms (13)— hover any for plain English
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Spastic paraparesis-deafness syndrome.

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No actively recruiting trials found for Spastic paraparesis-deafness syndrome at this time.

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No specialists are currently listed for Spastic paraparesis-deafness syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Spastic paraparesis-deafness syndrome.

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Community

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is the expected rate of progression for my (or my child's) symptoms?,Are there genetic tests that could help identify the exact cause in our family?,What medications or therapies can help manage the leg stiffness?,What type of hearing support would be most helpful at this stage?,Are there any clinical trials or research studies we could participate in?,What specialists should be part of our care team?,What can we do at home to maintain mobility and quality of life?

Common questions about Spastic paraparesis-deafness syndrome

What is Spastic paraparesis-deafness syndrome?

Spastic paraparesis-deafness syndrome is an extremely rare inherited neurological condition that combines progressive stiffness and weakness in the legs (spastic paraparesis) with hearing loss (deafness or sensorineural hearing impairment). The disease affects the nervous system in two main ways: it damages the nerve pathways that control leg movement, leading to increasing difficulty with walking and leg stiffness, and it impairs the nerves or structures involved in hearing. Patients typically notice gradual stiffening of the legs, trouble walking, and progressive hearing loss that may begin

How is Spastic paraparesis-deafness syndrome inherited?

Spastic paraparesis-deafness syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.